Despite rivals’ setbacks in Huntington’s, Alnylam and Regeneron are planning a pivotal trial of their RNA drug after encouraging early data.
endpoints.newsAlnylam plans bigger study of RNA drug for Huntington’s disease, despite failures in the fieldAlnylam & Regeneron's siRNA therapy brezosiran reduced mutant huntingtin protein 60-64% in 9 patients, spurring plans for a pivotal trial after Roche's tominersen failed.
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